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In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency.

Mahiny, Azita J
; 
Dewerth, Alexander
; 
Mays, Lauren E
; 
Alkhaled, Mohammed
; 
Mothes, Benedikt
; 
Malaeksefat, Emad
; 
Loretz, Brigitta
; 
Rottenberger, Jennifer
; 
Brosch, Darina M
; 
Reautschnig, Philipp
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2015-06
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Abstract
Citation
In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency. 2015, 33 (6):584-6 Nat. Biotechnol.
Affiliation
Helmholtz Institute for Pharmaceutical Research Saarland (HIPS)
Publisher
Journal
Nature biotechnology
URI
http://hdl.handle.net/10033/566264
DOI
10.1038/nbt.3241
PubMed ID
25985262
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Article
Language
en
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ISSN
1546-1696
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publications of the research group drug delivery ([HIPS] DDEL)